Is gene therapy available for people with Alpha-mannosidosis?
As of June 2019 there is no gene therapy available for treatment of people with Alpha-mannosidosis. However, gene therapy done in humans with Alpha-mannosidosis may be a possibility for treatment in the future. There are some research studies that show that gene therapy was helpful in treating Alpha-mannosidosis in cats with this condition.
SOURCE: Emory University - Department of Human Genetics in collaboration with ThinkGenetic • https://www.thinkgenetic.com/diseases/mannosidosis-alpha-b-lysosomal/living-with/9979 • DATE UPDATED: 2019-05-30