Alpha-mannosidosis

Living with

Is gene therapy available for people with Alpha-mannosidosis?

As of June 2019 there is no gene therapy available for treatment of people with Alpha-mannosidosis. However, gene therapy done in humans with Alpha-mannosidosis may be a possibility for treatment in the future. There are some research studies that show that gene therapy was helpful in treating Alpha-mannosidosis in cats with this condition.

SOURCE: Emory University - Department of Human Genetics in collaboration with ThinkGenetic • https://www.thinkgenetic.com/diseases/mannosidosis-alpha-b-lysosomal/living-with/9979 • DATE UPDATED: 2019-05-30

References

http://www.ncbi.nlm.nih.gov/books/NBK1396/

http://www.ncbi.nlm.nih.gov/pubmed/26354342

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